The Committee for Orphan Medicinal Products, a branch of the European Medicines Agency (EMA), favours than designating SLS-005 (trehalose) an orphan drug as a potential treatment for Sanfilippo syndrome, Seelos Therapeutics, its developer, announced.
Potential Sanfilippo Treatment, SLS-005, Advances as Orphan Drug in EU
Updated: Jul 24, 2020